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open question

Is progranulin replacement sufficient, or has irreversible neurodegeneration already occurred by the time patients are enrolled?

Open Question open Wiki: diseases-ftd
Is progranulin replacement sufficient, or has irreversible neurodegeneration already occurred by the time patients are enrolled?
Importance Elo
1500
Field Rank
Rank #231 in diseases
Tractability
0.50
Potential Impact
0.50
Evidence Summary
Extracted from wiki page diseases-ftd
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