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paper

AAV Capsid-Promoter Interactions Determine CNS Cell-Selective Gene Expression In Vivo.

📄 Paper Details
AAV Capsid-Promoter Interactions Determine CNS Cell-Selective Gene Expression In Vivo.
["Powell S", "Samulski R", "McCown T"]
Molecular therapy : the journal of the American Society of Gene Therapy PubMed DOI
Abstract

Cell-selective gene expression comprises a critical element of many adeno-associated virus (AAV) vector-based gene therapies, and to date achieving this goal has focused on AAV capsid engineering, cell-specific promoters, or cell-specific enhancers. Recently, we discovered that the capsid of AAV9 exerts a differential influence on constitutive promoters of sufficient magnitude to alter cell type gene expression in the rat CNS. For AAV9 vectors chicken β-actin (CBA) promoter-driven gene expressio...

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