{"artifact":{"id":"experiment-exp-wiki-experiments-crispr-gene-correction-cbs-psp","artifact_type":"experiment","entity_ids":null,"title":"CRISPR Gene Correction Approaches for CBS/PSP","quality_score":0.675,"created_by":"crosslink-v2","provenance_chain":null,"content_hash":null,"metadata":{"source":{"type":"manual","source_name":"wiki","extracted_by":"backfill_v1","extraction_date":"2026-04-16T01:00:16.905522Z"},"summary":"# CRISPR Gene Correction Approaches for CBS/PSP\n## Background and Rationale\nCRISPR-Cas9 gene editing represents a transformative therapeutic modality for treating monogenic forms of neurodegeneration, offering unprecedented precision for correcting disease-causing mutations at their genomic source. Progressive supranuclear palsy (PSP) and corticobasal syndrome (CBS) include several genetic variants caused by mutations in MAPT (microtubule-associated protein tau), GRN (granulin), and C9orf72 gene","entities":{"genes":["CRISPR"],"diseases":["Parkinson's Disease"]},"model_system":"human","_schema_version":1,"experiment_type":"clinical","primary_outcome":"Validate CRISPR Gene Correction Approaches for CBS/PSP","methodology_notes":"**Phase 1: Patient Recruitment and Screening (Months 1-6)**\n• Recruit 60 patients with genetically confirmed CBS/PSP (MAPT, GRN, or C9orf72 mutations)\n• Obtain informed consent for research participation and genetic analysis\n• Collect detailed clinical assessments using PSP Rating Scale and CBS severity measures\n• Extract peripheral blood mononuclear cells (PBMCs) and establish patient-specific iPSC lines\n• Perform whole genome sequencing to confirm pathogenic variants\n\n**Phase 2: CRISPR Design and Validation (Months 3-9)**\n• Design patient-specific guide RNAs targeting pathogenic mutations using CHOPCHOP and Benchling\n• Synthesize Cas9-RNP complexes with homology-directed repair (HDR) templates\n• Test editing efficiency in patient iPSCs using digital droplet PCR and Sanger sequencing\n• Validate off-target effects using GUIDE-seq and targeted amplicon sequencing\n• Optimize electroporation conditions for >70% editing efficiency\n\n**Phase 3: Neuronal Differentiation and Correction (Months","replication_status":"single_study","extraction_metadata":{"backfill_at":"2026-04-16T01:00:16.905527","needs_review":true,"extraction_notes":"Backfilled from wiki source (no PMID 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CBS"},{"source_artifact_id":"wiki-organizations-psp-germany","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-therapeutics-crispr-gene-editing-neurodegeneration","link_type":"mentions","strength":0.8,"evidence":"Gene target: CRISPR"},{"source_artifact_id":"wiki-mechanisms-cbs-frontal-cortical-involvement","link_type":"mentions","strength":0.7,"evidence":"Gene mention: CBS"},{"source_artifact_id":"wiki-therapeutics-ad-rna-therapeutics-companies","link_type":"mentions","strength":0.7,"evidence":"Gene mention: RNA"},{"source_artifact_id":"wiki-therapeutics-crispr-gene-editing-parkinsons","link_type":"mentions","strength":0.8,"evidence":"Gene target: CRISPR"},{"source_artifact_id":"wiki-mechanisms-psp-liquid-liquid-phase-separation-biomolecular-condensates","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-entities-mapt","link_type":"mentions","strength":0.7,"evidence":"Gene mention: 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PSP"},{"source_artifact_id":"wiki-mechanisms-psp-therapeutic-response-monitoring","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-mechanisms-psp-brainstem-circuit-vulnerability","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-mechanisms-mapt-tau-aggregation-psp-causal-chain","link_type":"mentions","strength":0.7,"evidence":"Gene mention: MAPT"},{"source_artifact_id":"wiki-mechanisms-cbs-psp-panxoneopathy-membrane-biology","link_type":"mentions","strength":0.7,"evidence":"Gene mention: CBS"},{"source_artifact_id":"wiki-therapeutics-rna-targeting-therapies-neurodegeneration","link_type":"mentions","strength":0.7,"evidence":"Gene mention: RNA"},{"source_artifact_id":"wiki-mechanisms-psp-lysosomal-dysfunction-autophagy-impairment","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-mechanisms-psp-serotonergic-dysfunction","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-organizations-psp-netherlands","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-diseases","link_type":"mentions","strength":0.6,"evidence":"Title match: Diseases"},{"source_artifact_id":"wiki-proteins-grn","link_type":"mentions","strength":0.7,"evidence":"Gene mention: GRN"},{"source_artifact_id":"wiki-clinical-trials-cbs-natural-history-nct06691234","link_type":"mentions","strength":0.7,"evidence":"Gene mention: CBS"},{"source_artifact_id":"wiki-investment-rna-therapeutics","link_type":"mentions","strength":0.7,"evidence":"Gene mention: RNA"},{"source_artifact_id":"wiki-organizations-psp-france","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-diagnostics-cbs-psp-multimodal-diagnosis","link_type":"mentions","strength":0.7,"evidence":"Gene mention: CBS"},{"source_artifact_id":"wiki-gaps-cbs-psp-tau-strain-biomarker-validation","link_type":"mentions","strength":0.7,"evidence":"Gene mention: CBS"},{"source_artifact_id":"wiki-mechanisms-rna-granule-dysfunction-neurodegeneration","link_type":"mentions","strength":0.7,"evidence":"Gene mention: RNA"},{"source_artifact_id":"wiki-clinical-trials-psp-clinical-trial-platform-nct07173803","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-mechanisms-psp-cbs-phenotypic-divergence-mechanism","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-mechanisms-psp-tau-conformation-pet-imaging-correlations","link_type":"mentions","strength":0.7,"evidence":"Gene mention: 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PSP"},{"source_artifact_id":"wiki-organizations-psp-uk","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-genes-mapt-haplotypes","link_type":"mentions","strength":0.7,"evidence":"Gene mention: MAPT"},{"source_artifact_id":"wiki-mechanisms-psp-glymphatic-system-dysfunction","link_type":"mentions","strength":0.7,"evidence":"Gene mention: PSP"},{"source_artifact_id":"wiki-therapeutics-rnai-therapies-neurodegeneration","link_type":"mentions","strength":0.7,"evidence":"Gene mention: RNA"},{"source_artifact_id":"wiki-proteins-mapt-protein","link_type":"mentions","strength":0.7,"evidence":"Gene mention: MAPT"},{"source_artifact_id":"wiki-mechanisms-rna-metabolism-dysregulation","link_type":"mentions","strength":0.7,"evidence":"Gene mention: RNA"},{"source_artifact_id":"wiki-genes-spr","link_type":"mentions","strength":0.6,"evidence":"Title match: SPR 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CRISPR mentioned 11x in wiki/therapeutics"},{"source_artifact_id":"wiki-technologies","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 7x in wiki/technologies"},{"source_artifact_id":"wiki-therapeutics-gene-therapy","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 7x in wiki/therapeutics-gene-therapy"},{"source_artifact_id":"wiki-therapeutics-fus-als-treatment","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/therapeutics-fus-als-treatment"},{"source_artifact_id":"wiki-therapeutics-section-107-crispr-therapies-cbs-psp","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 29x in wiki/therapeutics-section-107-crispr-therapies-cbs-psp"},{"source_artifact_id":"wiki-therapeutics-als-therapeutic-landscape","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/therapeutics-als-therapeutic-landscape"},{"source_artifact_id":"wiki-therapeutics-gene-therapy-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/therapeutics-gene-therapy-neurodegeneration"},{"source_artifact_id":"wiki-therapeutics-huntington-disease-treatment","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/therapeutics-huntington-disease-treatment"},{"source_artifact_id":"wiki-therapeutics-aav-vectors-neurodegenerative-gene-therapy","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/therapeutics-aav-vectors-neurodegenerative-gene-therapy"},{"source_artifact_id":"wiki-therapeutics-personalized-treatment-plan-atypical-parkinsonism","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in 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wiki/therapeutics-niemann-pick-disease-treatment"},{"source_artifact_id":"wiki-therapeutics-gene-silencing-therapy","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/therapeutics-gene-silencing-therapy"},{"source_artifact_id":"wiki-therapeutics-section-113-emerging-gene-therapy-cbs-psp","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 10x in wiki/therapeutics-section-113-emerging-gene-therapy-cbs-psp"},{"source_artifact_id":"wiki-therapeutics-antisense-therapy-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/therapeutics-antisense-therapy-neurodegeneration"},{"source_artifact_id":"wiki-therapeutics-tau-gene-therapy","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/therapeutics-tau-gene-therapy"},{"source_artifact_id":"wiki-therapeutics-section-253-advanced-optogenetics-chemogenetics-cbs-psp","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/therapeutics-section-253-advanced-optogenetics-chemogenetics-cbs-psp"},{"source_artifact_id":"wiki-therapeutics-friedreich-ataxia-treatment","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/therapeutics-friedreich-ataxia-treatment"},{"source_artifact_id":"wiki-therapeutics-nurr1-agonists-parkinsons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/therapeutics-nurr1-agonists-parkinsons"},{"source_artifact_id":"wiki-therapeutics-brain-drug-delivery-challenges","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/therapeutics-brain-drug-delivery-challenges"},{"source_artifact_id":"wiki-therapeutics-section-203-advanced-epigenetic-chromatin-therapy-cbs-psp","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/therapeutics-section-203-advanced-epigenetic-chromatin-therapy-cbs-psp"},{"source_artifact_id":"wiki-therapeutics-epigenetic-editing-crispr-cbs-psp","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 13x in wiki/therapeutics-epigenetic-editing-crispr-cbs-psp"},{"source_artifact_id":"wiki-therapeutics-nurr1-agonist-therapies","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/therapeutics-nurr1-agonist-therapies"},{"source_artifact_id":"wiki-clinical-trials-nimodipine-als","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/clinical-trials-nimodipine-als"},{"source_artifact_id":"wiki-clinical-trials-etx101-encoded-therapeutics-dravet-syndrome","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 6x in wiki/clinical-trials-etx101-encoded-therapeutics-dravet-syndrome"},{"source_artifact_id":"wiki-clinical-trials-nyscf-biobank-neurodegeneration-nct06203106","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/clinical-trials-nyscf-biobank-neurodegeneration-nct06203106"},{"source_artifact_id":"wiki-clinical-trials-amiloride-als","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/clinical-trials-amiloride-als"},{"source_artifact_id":"wiki-clinical-trials-cnversyt-megan-rodney","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/clinical-trials-cnversyt-megan-rodney"},{"source_artifact_id":"wiki-hypotheses-apoe-contributes-alzheimer's-disease-regulat","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/hypotheses-apoe-contributes-alzheimer's-disease-regulat"},{"source_artifact_id":"wiki-ideas-payload-aav-capsid-engineering-cns-therapy","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/ideas-payload-aav-capsid-engineering-cns-therapy"},{"source_artifact_id":"wiki-ideas-novel-therapy-index","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/ideas-novel-therapy-index"},{"source_artifact_id":"wiki-ideas-payload-base-editing-apoe4","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/ideas-payload-base-editing-apoe4"},{"source_artifact_id":"wiki-ideas-payload-ipsc-microglia-therapy","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 5x in wiki/ideas-payload-ipsc-microglia-therapy"},{"source_artifact_id":"wiki-ideas-payload-crispri-snca-silencing","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 6x in wiki/ideas-payload-crispri-snca-silencing"},{"source_artifact_id":"wiki-ideas-payload-escrthost-iii-neuroprotection-therapy","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/ideas-payload-escrthost-iii-neuroprotection-therapy"},{"source_artifact_id":"wiki-ideas-rankings","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/ideas-rankings"},{"source_artifact_id":"wiki-ideas-circrna-dysfunction-restoration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 5x in wiki/ideas-circrna-dysfunction-restoration"},{"source_artifact_id":"wiki-investment-gene-therapy","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 12x in wiki/investment-gene-therapy"},{"source_artifact_id":"wiki-investment-lrrk2-therapeutics","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/investment-lrrk2-therapeutics"},{"source_artifact_id":"wiki-investment-gene-therapy-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/investment-gene-therapy-neurodegeneration"},{"source_artifact_id":"wiki-investment-epigenetic-therapy-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/investment-epigenetic-therapy-neurodegeneration"},{"source_artifact_id":"wiki-investment-neurodegeneration-investment-funds","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/investment-neurodegeneration-investment-funds"},{"source_artifact_id":"wiki-cell-types-betz-cells-hsp","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-betz-cells-hsp"},{"source_artifact_id":"wiki-cell-types-tdp43-proteinopathy","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-tdp43-proteinopathy"},{"source_artifact_id":"wiki-cell-types-snca-a53t-neurons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-snca-a53t-neurons"},{"source_artifact_id":"wiki-cell-types-fragile-x-neurons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-fragile-x-neurons"},{"source_artifact_id":"wiki-cell-types-hek293","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/cell-types-hek293"},{"source_artifact_id":"wiki-cell-types-ipsc-derived-microglia","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/cell-types-ipsc-derived-microglia"},{"source_artifact_id":"wiki-cell-types-engineered-neuronal-cells","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/cell-types-engineered-neuronal-cells"},{"source_artifact_id":"wiki-cell-types-unfolded-protein-response-neurons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-unfolded-protein-response-neurons"},{"source_artifact_id":"wiki-cell-types-spinal-ventral-horn-neurons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-spinal-ventral-horn-neurons"},{"source_artifact_id":"wiki-cell-types-retinal-ganglion-cells-glaucoma","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-retinal-ganglion-cells-glaucoma"},{"source_artifact_id":"wiki-cell-types-schwann-cells-peripheral-neuropathy","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/cell-types-schwann-cells-peripheral-neuropathy"},{"source_artifact_id":"wiki-cell-types-rett-syndrome-neurons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-rett-syndrome-neurons"},{"source_artifact_id":"wiki-cell-types-huntingtons-disease-medium-spiny-neurons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-huntingtons-disease-medium-spiny-neurons"},{"source_artifact_id":"wiki-genes-pde1b","link_type":"mentions","strength":0.4,"evidence":null},{"source_artifact_id":"wiki-cell-types-oxytocin-receptor-neurons","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/cell-types-oxytocin-receptor-neurons"},{"source_artifact_id":"wiki-cell-types-potassium-channel-neurons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-potassium-channel-neurons"},{"source_artifact_id":"wiki-cell-types-parkin-deficient-dopaminergic-neurons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-parkin-deficient-dopaminergic-neurons"},{"source_artifact_id":"wiki-cell-types-pink1-deficient-dopamine","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-pink1-deficient-dopamine"},{"source_artifact_id":"wiki-cell-types-gene-edited-neurons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/cell-types-gene-edited-neurons"},{"source_artifact_id":"wiki-cell-types-knockout-cells","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/cell-types-knockout-cells"},{"source_artifact_id":"wiki-mechanisms-epigenetics-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 6x in wiki/mechanisms-epigenetics-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-ftd-tdp43-pathway","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-ftd-tdp43-pathway"},{"source_artifact_id":"wiki-mechanisms-synaptic-vesicle-trafficking","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-synaptic-vesicle-trafficking"},{"source_artifact_id":"wiki-mechanisms-epigenetics-ad","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/mechanisms-epigenetics-ad"},{"source_artifact_id":"wiki-mechanisms-dipeptide-repeat-proteins","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-dipeptide-repeat-proteins"},{"source_artifact_id":"wiki-mechanisms-abca7-lipid-transport-microglial-phagocytosis-ad-causal-chain","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-abca7-lipid-transport-microglial-phagocytosis-ad-causal-chain"},{"source_artifact_id":"wiki-mechanisms-neurexin-neuroligin-neurodegeneration-modulation","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-neurexin-neuroligin-neurodegeneration-modulation"},{"source_artifact_id":"wiki-mechanisms-animal-models-cbs","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-animal-models-cbs"},{"source_artifact_id":"wiki-mechanisms-huntingtons-disease-pathway","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-huntingtons-disease-pathway"},{"source_artifact_id":"wiki-mechanisms-htt-huntingtin-hd-causal-chain","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/mechanisms-htt-huntingtin-hd-causal-chain"},{"source_artifact_id":"wiki-mechanisms-vps35-pathway-parkinsons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-vps35-pathway-parkinsons"},{"source_artifact_id":"wiki-mechanisms-autophagy-molecular-regulation","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-autophagy-molecular-regulation"},{"source_artifact_id":"wiki-mechanisms-centrosome-dysfunction","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-centrosome-dysfunction"},{"source_artifact_id":"wiki-mechanisms-tgf-beta-hs3st2-tau-axis","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-tgf-beta-hs3st2-tau-axis"},{"source_artifact_id":"wiki-mechanisms-tauopathies","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-tauopathies"},{"source_artifact_id":"wiki-mechanisms-transcription-regulation-neurodegeneration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-transcription-regulation-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-prion-protein-metabolism","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-prion-protein-metabolism"},{"source_artifact_id":"wiki-mechanisms-macroautophagy-dysfunction-validation-pd","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-macroautophagy-dysfunction-validation-pd"},{"source_artifact_id":"wiki-mechanisms-histone-modification-pathway-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-histone-modification-pathway-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-synaptic-vesicle-cycling-neurodegeneration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-synaptic-vesicle-cycling-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-camp-signaling-neurodegeneration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-camp-signaling-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-fbxo7-mitophagy-pd-causal-chain","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-fbxo7-mitophagy-pd-causal-chain"},{"source_artifact_id":"wiki-mechanisms-rab39b-endosomal-lysosomal-pd-causal-chain","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-rab39b-endosomal-lysosomal-pd-causal-chain"},{"source_artifact_id":"wiki-mechanisms-mhtt-clearance-mechanisms","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 11x in wiki/mechanisms-mhtt-clearance-mechanisms"},{"source_artifact_id":"wiki-mechanisms-mptp-parkinson-model","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-mptp-parkinson-model"},{"source_artifact_id":"wiki-mechanisms-chondrogenesis","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-chondrogenesis"},{"source_artifact_id":"wiki-genes-pfn1","link_type":"mentions","strength":0.4,"evidence":null},{"source_artifact_id":"wiki-mechanisms-mid1-huntingtons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-mid1-huntingtons"},{"source_artifact_id":"wiki-mechanisms-syk-kinase-microglial-activation-alzheimers","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-syk-kinase-microglial-activation-alzheimers"},{"source_artifact_id":"wiki-mechanisms-novel-therapeutic-modalities-synthesis","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 6x in wiki/mechanisms-novel-therapeutic-modalities-synthesis"},{"source_artifact_id":"wiki-mechanisms-pink1-parkin-mitophagy-pathway-parkinsons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-pink1-parkin-mitophagy-pathway-parkinsons"},{"source_artifact_id":"wiki-mechanisms-mitochondrial-dynamics-neurodegeneration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-mitochondrial-dynamics-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-alpha-synuclein-clearance","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-alpha-synuclein-clearance"},{"source_artifact_id":"wiki-mechanisms-jnk-p38-mapk-parkinsons","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-jnk-p38-mapk-parkinsons"},{"source_artifact_id":"wiki-mechanisms-hd-ion-channel-dysfunction","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-hd-ion-channel-dysfunction"},{"source_artifact_id":"wiki-mechanisms-epigenetic-alterations-ad","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-epigenetic-alterations-ad"},{"source_artifact_id":"wiki-mechanisms-trem2-microglial-dysfunction-ad-causal-chain","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-trem2-microglial-dysfunction-ad-causal-chain"},{"source_artifact_id":"wiki-mechanisms-chromatin-remodeling-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-chromatin-remodeling-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-ad-pd-shared-proteinostasis-failure","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-ad-pd-shared-proteinostasis-failure"},{"source_artifact_id":"wiki-mechanisms-prime-editing-neurodegenerative-diseases","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 9x in wiki/mechanisms-prime-editing-neurodegenerative-diseases"},{"source_artifact_id":"wiki-mechanisms-adult-neurogenesis-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-adult-neurogenesis-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-chromatin-remodeling-epigenetic-therapy-neurodegeneration-synthesis","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/mechanisms-chromatin-remodeling-epigenetic-therapy-neurodegeneration-synthesis"},{"source_artifact_id":"wiki-mechanisms-cellular-reprogramming-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-cellular-reprogramming-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-uchl1-park5-pathway","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-uchl1-park5-pathway"},{"source_artifact_id":"wiki-mechanisms-epigenetic-clocks-brain-aging","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-epigenetic-clocks-brain-aging"},{"source_artifact_id":"wiki-mechanisms-chemokine-signaling-neurodegeneration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-chemokine-signaling-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-physiological-amyloidogenesis-enzymes","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-physiological-amyloidogenesis-enzymes"},{"source_artifact_id":"wiki-mechanisms-gba-parkinson-risk","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-gba-parkinson-risk"},{"source_artifact_id":"wiki-mechanisms-splice-modulation-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 6x in wiki/mechanisms-splice-modulation-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-dopamine-pathway","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-dopamine-pathway"},{"source_artifact_id":"wiki-mechanisms-aav-gene-therapy-vectors-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-aav-gene-therapy-vectors-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-gba-pathway-parkinsons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-gba-pathway-parkinsons"},{"source_artifact_id":"wiki-mechanisms-proteostasis-network-comparison","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-proteostasis-network-comparison"},{"source_artifact_id":"wiki-mechanisms-lrrk2-signaling-pathway","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-lrrk2-signaling-pathway"},{"source_artifact_id":"wiki-mechanisms-fus-als-ftd-causal-chain","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-fus-als-ftd-causal-chain"},{"source_artifact_id":"wiki-mechanisms-optn-mitophagy-neurodegeneration-causal-chain","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/mechanisms-optn-mitophagy-neurodegeneration-causal-chain"},{"source_artifact_id":"wiki-mechanisms-gba-lysosomal-function-parkinsons","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-gba-lysosomal-function-parkinsons"},{"source_artifact_id":"wiki-mechanisms-notch-signaling-neurodegeneration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-notch-signaling-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-mhtt-clearance","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 8x in wiki/mechanisms-mhtt-clearance"},{"source_artifact_id":"wiki-mechanisms-selective-neuronal-vulnerability","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-selective-neuronal-vulnerability"},{"source_artifact_id":"wiki-mechanisms-huntingtin-aggregation","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-huntingtin-aggregation"},{"source_artifact_id":"wiki-mechanisms-als-molecular-subtypes","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-als-molecular-subtypes"},{"source_artifact_id":"wiki-mechanisms-spliceosome","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-spliceosome"},{"source_artifact_id":"wiki-genes-kcnip3","link_type":"mentions","strength":0.4,"evidence":null},{"source_artifact_id":"wiki-mechanisms-autophagy-lysosome-pathway","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-autophagy-lysosome-pathway"},{"source_artifact_id":"wiki-mechanisms-trinucleotide-repeat-expansion","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-trinucleotide-repeat-expansion"},{"source_artifact_id":"wiki-mechanisms-nanomedicine-alzheimers-disease","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-nanomedicine-alzheimers-disease"},{"source_artifact_id":"wiki-mechanisms-epigenetics-als","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-epigenetics-als"},{"source_artifact_id":"wiki-mechanisms-c9orf72-als-network","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-c9orf72-als-network"},{"source_artifact_id":"wiki-mechanisms-focused-ultrasound-drug-delivery-brain","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-focused-ultrasound-drug-delivery-brain"},{"source_artifact_id":"wiki-mechanisms-chromatin-remodeling","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-chromatin-remodeling"},{"source_artifact_id":"wiki-mechanisms-epigenetics-parkinsons","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 6x in wiki/mechanisms-epigenetics-parkinsons"},{"source_artifact_id":"wiki-mechanisms-peroxisome-neurodegeneration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-peroxisome-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-autophagy-lysosomal-impairment-comparison","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-autophagy-lysosomal-impairment-comparison"},{"source_artifact_id":"wiki-mechanisms-remyelination","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-remyelination"},{"source_artifact_id":"wiki-mechanisms-biomolecular-condensates-neurodegeneration","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-biomolecular-condensates-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-epigenetic-dysregulation-comparison","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/mechanisms-epigenetic-dysregulation-comparison"},{"source_artifact_id":"wiki-mechanisms-neuronal-migration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-neuronal-migration"},{"source_artifact_id":"wiki-mechanisms-peroxisomal-dysfunction","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 4x in wiki/mechanisms-peroxisomal-dysfunction"},{"source_artifact_id":"wiki-mechanisms-neurogenesis-neurodegeneration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in wiki/mechanisms-neurogenesis-neurodegeneration"},{"source_artifact_id":"wiki-mechanisms-trem2","link_type":"mentions","strength":0.5,"evidence":"Content: CRISPR mentioned 3x in wiki/mechanisms-trem2"},{"source_artifact_id":"wiki-mechanisms-lncrna-signaling-neurodegeneration","link_type":"mentions","strength":0.44999999999999996,"evidence":"Content: CRISPR mentioned 2x in 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