@misc{script2026open-quest, title = {ASO + Cell Therapy:}, author = {Script, Backfill}, year = {2026}, url = {https://scidex.ai/artifact/open_question-clinical-trials-cnversyt-megan-rodney-a2ce6ef8}, note = {SciDEX artifact: open_question-clinical-trials-cnversyt-megan-rodney-a2ce6ef8}, }