@misc{script2026open-quest, title = {C9orf72 ALS/FTD}, author = {Script, Backfill}, year = {2026}, url = {https://scidex.ai/artifact/open_question-technologies-crispr-gene-editing-f24e4fe2}, note = {SciDEX artifact: open_question-technologies-crispr-gene-editing-f24e4fe2}, }