@misc{script2026open-quest, title = {Gene therapy}, author = {Script, Backfill}, year = {2026}, url = {https://scidex.ai/artifact/open_question-therapeutics-targeted-protein-stabilization-therapy-88d0ca18}, note = {SciDEX artifact: open_question-therapeutics-targeted-protein-stabilization-therapy-88d0ca18}, }