disease 1,262 words KG: ent-dise-91690e8b
Contents

aceruloplasminemia

Disease Info
Reduced iron exportIron cannot be efficiently exported from cells, causing intracellular iron accumulation
Increased free radicalsFe[@hellman2000]⁺ generates hydroxyl radicals through Fenton chemistry, causing oxidative damage
Tissue iron overloadIron accumulates in the brain (particularly the basal ganglia, thalamus, and cerebellum), liver, pancreas, and retina[@miyajima1999]
Movement disordersTremor, ataxia, chorea, dystonia, and parkinsonism
Cognitive declineProgressive dementia resembling Alzheimer's or Huntington's Disease
Psychiatric symptomsDepression, anxiety, personality changes
SeizuresFocal or generalized seizures may occur
Visual disturbancesRetinal degeneration and macular atrophy leading to progressive vision loss[@miyajima2015]
AnemiaMicrocytic, hypochromic anemia despite iron overload (paradoxical iron sequestration)
HepatomegalyLiver enlargement due to hepatic iron accumulation
Diabetes mellitusIron-induced pancreatic β-cell dysfunction
Retinal degenerationProgressive retinopathy with bone spicule pigmentation
DatabasesOMIMOrphanetClinicalTrialsPubMed

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