disease 3,181 words KG: ent-dise-26f3cf5a 2026-03-23
kind:diseasesection:diseasesstate:published
Contents

Cockayne Syndrome

Disease Info
PrevalenceApproximately 1 in 200,000 births in Western Europe (Kleijer et al., 2008)
Typical OnsetLater childhood to adolescence
Higher prevalence regionsFounder effects have been noted in some isolated populations
Sex distributionAffects males and females equally (autosomal recessive)
Complementation groups~80% of patients belong to the CS-B group (ERCC6 mutations); ~20% to the CS-A group (ERCC8 mutations)
Carrier frequencyEstimated at approximately 1 in 250 in the general population
Key featuresMilder growth failure, preserved intellectual function for longer periods, photosensitivity, and slowly progressive neurological symptoms
CourseSlower progression than Types I and II
Life expectancyCan survive into the third decade or beyond
GeneticsAssociated with hypomorphic mutations in either CSA or CSB
StructureContains 7 conserved ATPase motifs characteristic of SWI2/SNF2 DNA-stimulated ATPases
FunctionCSB protein is a multifunctional protein involved in TC-NER, general transcription, chromatin remodeling, and mitochondrial maintenance
DatabasesOMIMOrphanetClinicalTrialsPubMed

Knowledge Graph

Related Hypotheses (23)

Nutrient-Sensing Epigenetic Circuit Reactivation
Score: 0.70
PARP1 Inhibition Therapy
Score: 0.58
Metabolic Reprogramming via Coordinated Multi-Gene CRISPR Ci
Score: 0.45
APOE-Dependent Autophagy Restoration
Score: 0.63
Digital Twin-Guided Metabolic Reprogramming
Score: 0.61

Related Analyses (5)

TDP-43 phase separation therapeutics for ALS-FTD
neurodegeneration · archived
Epigenetic reprogramming in aging neurons
neurodegeneration · archived
Autophagy-lysosome pathway convergence across neurodegenerat
neurodegeneration · archived
Protein aggregation cross-seeding across neurodegenerative d
neurodegeneration · archived
Metabolic reprogramming in neurodegenerative disease
neurodegeneration · completed

Related Experiments (2)

Gandouling protection against brain injury in Wilson's disea
validation · proposed · Score: 0.90
Epigenetic Clocks in Neurodegeneration — Causal Drivers or P
validation · proposed · Score: 0.40