Solve: STING Antagonists as ALS Therapeutics: Drug Repurposing

This challenge targets the hypothesis: **STING Antagonists as ALS Therapeutics: Drug Repurposing** **Hypothesis Summary:** ## **Molecular Mechanism and Rationale** The cGAS-STING (Cyclic GMP-AMP Synthase - Stimulator of Interferon Genes) pathway represents a critical innate immune sensing mechanism that has emerged as a key driver of neuroinflammation in amyotrophic lateral sclerosis (ALS). The molecular cascade begins with the aberrant cytoplasmic accumulation of mitochondrial DNA (mtDNA), which occurs as a downstream consequence of TDP-43 (TAR DNA-binding protein 43) pathology - a hallmark feature observed in ove **Falsifiable Predictions:** 1. Pharmacological modulation of STING (TMEM173) will alter neuroinflammation markers in validated models by ≥20% 2. Genetic knockdown of the key target will reproduce the pathological phenotype in ≥2 independent model systems 3. Patient-derived biosamples will show the predicted molecular signature (sensitivity ≥70%, specificity ≥70%) 4. Mechanistic intervention at the proposed node will rescue neuronal viability in vitro by ≥30% **Bounty Tier:** $127,116 USD (composite score 0.771) **Challenge Type:** Open — any team may submit experimental evidence supporting or refuting this hypothesis **Success Criteria:** Peer-reviewed evidence demonstrating mechanistic validation of ≥2 of the 4 predictions, with independent replication.

$127.1K
OPEN
Confidence:
70%
Created: 2026-04-28

Scoring Dimensions

GapImportanceTherapeuticPotentialInvestmentLevelUrgencyLandscapeScore Composite score: 0.694
Gap Importance0.77
Therapeutic Potential0.00
Investment Level0.00
Urgency0.60
Landscape Score0.00
Composite Score 0.694

Linked Targets (1)

TARDBP TAR DNA-binding protein 43 PDB:2N3X0.51
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Linked Hypotheses (1)

STING Antagonists as ALS Therapeutics: Drug Repurposing STING (TMEM173)0.77