Human filamin mutations and heterotopic neurons

Exploratory Score: 0.700 Price: $0.50 heterotopic neurons human patients Status: proposed

What This Experiment Tests

Exploratory experiment designed to discover new patterns targeting filamin in human patients. Primary outcome: presence of heterotopic neurons

Description

Analysis of human patients with filamin gene mutations to understand the role of this actin-associated protein in neuronal migration. The study examined how mutations in filamin, which is involved in leading edge extension during neuronal migration, result in heterotopic neurons (neurons located in abnormal positions). This represents a naturally occurring human genetic model for studying defective leading edge extension mechanisms during neuronal migration.

TARGET GENE
filamin
MODEL SYSTEM
human patients
ESTIMATED COST
$0
TIMELINE
0 months
PATHWAY
actin cytoskeleton/leading edge extension
SOURCE
extracted_from_pmid_11429281
PRIMARY OUTCOME
presence of heterotopic neurons

Scoring Dimensions

Info Gain 0.00 (25%) Feasibility 0.00 (20%) Hyp Coverage 0.00 (20%) Cost Effect. 0.00 (15%) Novelty 0.00 (10%) Ethical Safety 0.00 (10%) 0.700 composite

📖 Wiki Pages

Neuronal MigrationmechanismMechanismsindex

Protocol

genetic analysis and neuropathological examination of patients with filamin mutations

Expected Outcomes

mutations in filamin would cause defective leading edge extension leading to abnormal neuronal positioning

Success Criteria

demonstration of heterotopic neurons in patients with filamin mutations

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