iPSC-derived endothelial cell iron uptake with RLS CSF exposure

Exploratory Score: 0.900 Price: $0.50 restless legs syndrome iPSC-derived human endothelial cells Status: proposed

What This Experiment Tests

Exploratory experiment designed to discover new patterns targeting TfR1 in iPSC-derived human endothelial cells. Primary outcome: iron uptake and transport in endothelial cells

Description

This experiment investigated iron uptake and transport mechanisms in human endothelial cells (ECs) derived from induced pluripotent stem cells (iPSCs) when exposed to cerebrospinal fluid (CSF) from restless legs syndrome (RLS) patients versus controls. The study aimed to understand how RLS CSF affects blood-brain barrier endothelial cell iron handling, which is relevant to the brain iron deficiency observed in RLS. The researchers measured iron uptake, transport, and related molecular mechanisms including transferrin receptor 1 (TfR1) expression and miR-124-3p levels. The experiment revealed that RLS CSF decreased iron uptake and transport in ECs, and also decreased TfR1 protein expression through increased miR-124-3p binding that reduced TfR1 mRNA stability. This provides mechanistic insight into how brain iron deficiency develops in RLS through altered blood-brain barrier iron transport.

TARGET GENE
TfR1
MODEL SYSTEM
iPSC-derived human endothelial cells
ESTIMATED COST
$0
TIMELINE
0 months
PATHWAY
iron transport/transferrin receptor pathway
SOURCE
extracted_from_pmid_41947413
PRIMARY OUTCOME
iron uptake and transport in endothelial cells

Scoring Dimensions

Info Gain 0.00 (25%) Feasibility 0.00 (20%) Hyp Coverage 0.00 (20%) Cost Effect. 0.00 (15%) Novelty 0.00 (10%) Ethical Safety 0.00 (10%) 0.900 composite

📖 Wiki Pages

TFR1 GenegeneCSF-1R InhibitorstherapeuticCSF Dynamics and Glymphatic Therapy in CBS/PSPtherapeuticCSF and Blood Biomarkers in Progressive SupranuclemechanismCSF Cytokine Profiles as Parkinson's Disease BiomagapCSF Dynamic Biomarkers for Differential Diagnosis experimentCSF Dynamic Biomarkers for Differential Diagnosis experimentCSF and Blood Biomarkers in Progressive SupranuclebiomarkerCSF Synaptic Biomarker Panel for Neurodegenerativebiomarkercsf-pta181biomarkerCSF O-GlcNAc — Target Engagement Biomarker for OGAbiomarkerCSF Neurofilament Light Chain (NfL) in NeurodegenebiomarkerCSF Biomarker Comparison Across Neurodegenerative biomarkerCSF Biomarkers for Corticobasal Syndrome and ProgrbiomarkerResearchersindex

Protocol

Human endothelial cells generated from iPSCs were exposed to CSF from RLS patients (n=14) or controls (n=15). Iron uptake and transport were measured, along with TfR1 protein expression, mRNA stability, and miR-124-3p levels.

Expected Outcomes

RLS CSF would alter iron handling in endothelial cells consistent with brain iron deficiency

Success Criteria

Significant differences in iron uptake/transport between RLS CSF and control CSF treated cells

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