| Gene Symbol | ent-gene-694200ea |
| Drug | Company |
| Migalastat (Galafold) | Amicus |
| Ambroxol | Various |
| Venglustat (GZ161) | Sanofi |
| Trial | Phase |
| ambroxol-PD | Phase II |
| GBA-PD Natural History | Observational |
| Target | Approach |
| AADC | Enzyme replacement |
| GBA | Gene therapy/chaperone |
| LRRK2 | Kinase inhibitor |
| SNCA | ASO/siRNA |
| Approach | Status |
| IGF1 Peptide | Research |
| IGF1 Mimetics | Preclinical |
| KG Connections | 2 knowledge graph edges |
| Databases | GeneCardsUniProtNCBI GeneHPASTRING |