therapeutic 1,525 words KG: ent-gene-b254988d
section:therapeuticskind:therapeutictopic:parkinsons
Contents

USP30 Inhibitors for Parkinson's Disease

🔬 Protein Info
Gene Symbolent-gene-b254988d
Therapeutic EffectMechanism
Enhanced ubiquitinationPreservation of ubiquitin on OMM proteins
Increased receptor recruitmentp62, OPTN, NDP52 more efficiently recruited
Improved mitophagyMore efficient clearance of damaged mitochondria
Neuronal protectionReduced oxidative stress and apoptosis
Alpha-synuclein reductionImproved mitophagy decreases aggregation[@wang2023]
CompanyCompound
Denali TherapeuticsDNL309
DepYmedTH3289
Bristol Myers SquibbBMS-986467
RocheCompound 9
Academic consortiaVarious
Molecular weight<500 Da
Brain penetrationB/P ratio >1
Selectivity>100x vs other DUBs
KG Connections2 knowledge graph edges
DatabasesGeneCardsUniProtNCBI GeneHPASTRING

Knowledge Graph

Related Hypotheses (3)

The Mitochondrial-Lysosomal Metabolic Coupling Dysfunction
Score: 0.40
TFEB-PGC1α Mitochondrial-Lysosomal Decoupling
Score: 0.40
Prohibitin-2 Mitochondrial Cross-Seeding Hub Disruption
Score: 0.38

Related Analyses (17)

TREM2 agonism vs antagonism in DAM microglia
neurodegeneration · completed
TDP-43 phase separation therapeutics for ALS-FTD
neurodegeneration · archived
Blood-brain barrier transport mechanisms for antibody therap
neurodegeneration · archived
What are the mechanisms by which gut microbiome dysbiosis in
neurodegeneration · completed
What are the mechanisms by which gut microbiome dysbiosis in
neurodegeneration · archived

Related Experiments (30)

AAV Serotype Comparison for LRRK2 Knockdown in PD Gene Thera
validation · proposed · Score: 0.40
AAV-LRRK2 IND-Enabling Study Design
clinical · proposed · Score: 0.40
AAV Serotype Comparison for LRRK2 Knockdown in PD
validation · proposed · Score: 0.40
Alpha-Synuclein SAA Kinetics Study — Biological Staging Back
clinical · proposed · Score: 0.40
Alpha-Synuclein Aggregation Triggers — Sporadic PD Initiatio
clinical · proposed · Score: 0.40

Knowledge Graph (2 edges)

ent-gene-b254988d data_in benchmark_ot_ad_answer_key:USP30
benchmark_ot_ad_answer_key:USP30 data_in ent-gene-b254988d