entity

ASO

Entity Detail — Knowledge Graph Node

Understanding Entity Pages

This page aggregates everything SciDEX knows about ASO: its mechanistic relationships (Knowledge Graph edges), hypotheses targeting it, analyses mentioning it, and supporting scientific papers. The interactive graph below shows its immediate neighbors. All content is AI-synthesized from peer-reviewed literature.

6Connections
30Hypotheses
2Analyses
5Outgoing
1Incoming
6Experiments
4Debates

No AI portrait yet

Wiki Pages (16)

Knowledge base pages for this entity

Canonical Page

ASO Therapy for Parkinson's Disease

therapeutic · 2531 words

NIO752 (Roche ASO)

therapeutic · 2713 words

Personalized Antisense Oligonucleotide (ASO) Therapy

therapeutic · 2512 words

BIIB080 (MAPTRx) ASO Therapy for PSP

clinical · 2319 words

Section 174: Oligonucleotide Therapies (ASO/SSO) in CBS/PSP

therapeutic · 2108 words

Tau ASO Therapy

mechanism · 2083 words

Outgoing (5)

TargetRelationTypeStr
SNCAinhibitsgene0.87
ALPHA_SYNUCLEINinhibitsprotein0.87
TDP-43targetsprotein0.75
axonal degenerationpreventsphenotype0.70
PARKINSONS_DISEASEtreatsdisease0.64

Incoming (1)

SourceRelationTypeStr
TfR1bindsreceptor0.90

Targeting Hypotheses (30)

Hypotheses where this entity is a therapeutic target

HypothesisScoreDiseaseAnalysis
Closed-loop transcranial focused ultrasound targeting EC-II 0.968 alzheimers Circuit-level neural dynamics in neurode
Closed-loop transcranial focused ultrasound targeting EC-II 0.955 alzheimers Circuit-level neural dynamics in neurode
Closed-loop transcranial focused ultrasound to restore hippo 0.912 alzheimers Circuit-level neural dynamics in neurode
Closed-loop transcranial focused ultrasound to restore hippo 0.865 alzheimers Circuit-level neural dynamics in neurode
Closed-loop focused ultrasound targeting EC-II PV interneuro 0.863 alzheimers Circuit-level neural dynamics in neurode
Closed-loop transcranial focused ultrasound to restore hippo 0.827 alzheimers Circuit-level neural dynamics in neurode
Real-time gamma-guided transcranial focused ultrasound targe 0.827 alzheimers Circuit-level neural dynamics in neurode
Microglial AIM2 Inflammasome as the Primary Driver of TDP-43 0.824 neurodegeneration What are the mechanisms by which gut mic
Astrocyte-Intrinsic NLRP3 Inflammasome Activation by Alpha-S 0.822 neurodegeneration What are the mechanisms by which gut mic
Mitochondrial DAMPs-Driven AIM2 Inflammasome Activation in N 0.805 neurodegeneration What are the mechanisms by which gut mic
Calcium-Dysregulated mPTP Opening as an Alternative mtDNA Re 0.804 neurodegeneration What are the mechanisms by which gut mic
Targeting the Mechanistic Link Between AQP4 Dysfunction and 0.803 neurodegeneration Can ferroptosis inhibitors prevent BBB d
Mitochondrial DNA-Driven AIM2 Inflammasome Activation in Neu 0.803 neurodegeneration What are the mechanisms by which gut mic
NLRP3 inflammasome amplification across AD and PD proteinopa 0.800 multi Cross-disease neurodegeneration mechanis
Closed-loop transcranial focused ultrasound targeting CA1 PV 0.797 alzheimers Circuit-level neural dynamics in neurode
Closed-loop transcranial focused ultrasound to restore hippo 0.767 alzheimers Circuit-level neural dynamics in neurode
Focused Ultrasound with Microbubble Contrast Agents for Anti 0.762 neurodegeneration Blood-brain barrier antibody transport m
ASO-mediated reduction of toxic C9orf72 dipeptide repeat pro 0.760 neurodegeneration Test
Closed-loop focused ultrasound targeting CA1 PV interneurons 0.754 alzheimers Circuit-level neural dynamics in neurode
Closed-loop focused ultrasound targeting EC-II SST interneur 0.748 alzheimers Circuit-level neural dynamics in neurode
NLRP3 Inflammasome Inhibition for Neuroprotection in Parkins 0.720 neurodegeneration Test
ASO-Mediated Exon Skipping to Restore FUS-TAZ Chaperone Axis 0.720 neurodegeneration How does FUS loss-of-function in TAZ reg
C9orf72 ASO Treatment Reverses TDP-43 Pathology in ALS/FTD 0.720 neurodegeneration Test Hypothesis Fixtures
NLRP3 Inflammasome Lock Perpetuates Senescence-Associated In 0.720 neurodegeneration What molecular mechanisms drive microgli
VCP/p97 ATPase mutations impair extraction of ubiquitinated 0.720 neurodegeneration What are the neuron-specific effects of
Early Proteasome Restoration Therapy 0.712 neurodegeneration Gene expression changes in aging mouse b
GluN2B Tonic Activity Suppresses Glymphatic Perfusion Via Va 0.700 neuroscience GluN2B-Mediated Thalamocortical Control
TREM2 haploinsufficiency dysregulates microglial synaptic su 0.700 neurodegeneration Synaptic pruning by microglia in neurode
Closed-loop transcranial focused ultrasound to restore hippo 0.000 alzheimers Circuit-level neural dynamics in neurode
Closed-loop transcranial focused ultrasound with gamma entra 0.000 alzheimers Circuit-level neural dynamics in neurode

Mentioning Analyses (2)

Scientific analyses that reference this entity

RNA binding protein dysregulation across ALS FTD AD

neurodegeneration | 2026-04-13 | 2 hypotheses Top: 0.664

What are the conserved secondary structures in dilncRNAs that enable selective t

molecular biology | 2026-04-10 | 5 hypotheses Top: 0.657

Experiments (6)

Experimental studies targeting or related to this entity

ExperimentTypeDiseaseScoreFeasibilityModelStatusEst. Cost
Plant-based dietary patterns and Alzheimer's disease risk in multiethn clinical Alzheimer's disease and relate 0.950 0.00 human patients proposed N/A
Microglial SIRPα expression in human Alzheimer's disease tissue exploratory Alzheimer's disease 0.800 0.00 human brain tissue proposed N/A
Closed-loop tFUS Enhances Glymphatic Clearance and Restores CA1 PV Int in_vivo Alzheimer's disease 0.765 0.55 APP/PS1 mice 8-11 months (n=10 abandoned $125,000
tFUS Targeting EC-II SST Interneurons Restores Hippocampal-Prefrontal in_vivo Alzheimer's disease 0.744 0.48 hAPP-J20 mice (n=10/group x 3 abandoned $110,000
Anti-Tau Antibody vs ASO/Gene Therapy — Comparative Efficacy in 4R-Tau validation Neurodegeneration 0.400 0.50 cell_line proposed $170,000
Tau ASO Therapy validation Alzheimer's Disease 0.400 0.50 human proposed $2,280,000

Related Papers (19)

Scientific publications cited in analyses involving this entity

Title & PMIDAuthorsJournalYearCitations
Small molecule-driven NLRP3 inflammation inhibition via interplay between ubiqui [PMID:30966861] ["Han X", "Sun S", "Sun Y", "Song Q", "Z Autophagy 2020 1
Retinal Müller glia alterations and their impact on ocular glymphatic clearance [PMID:41603340] Das G, Raghunathan R, Wang L J Alzheimers Dis 2026 0
The Glymphatic-Venous Axis in Brain Clearance Failure: Aquaporin-4 Dysfunction, [PMID:41226584] ["Costea D", "Dobrin N", "Tataru C", "To International journal of molec 2025 0
Longitudinal changes of blood-brain barrier and transcytolemmal water exchange p [PMID:40089221] Xiong C, Yu Z, Yin Y Neuroimage 2025 0
The future of biomarkers for vascular contributions to cognitive impairment and [PMID:40542975] Lennon MJ, Karvelas N, Ganesh A Geroscience 2025 0
P-tau217 correlates with neurodegeneration in Alzheimer's disease, and targeting [PMID:38513667] Zhang D, Zhang W, Ming C, Gao X, Yuan H, Neuron 2024 0
The necroptosis cell death pathway drives neurodegeneration in Alzheimer's disea [PMID:38852117] Balusu S, De Strooper B Acta neuropathologica 2024 0
Inhibition of autophagy in microglia and macrophages exacerbates innate immune r [PMID:36652438] Hegdekar N, Sarkar C, Bustos S, Ritzel R Autophagy 2023 0
Parkin regulates microglial NLRP3 and represses neurodegeneration in Parkinson's [PMID:37029500] Yan YQ, Zheng R, Liu Y, Ruan Y, Lin ZH, Aging cell 2023 0
Inflammasome assembly in neurodegenerative diseases. [PMID:37633753] Singh J, Habean ML, Panicker N Trends in neurosciences 2023 0
Microglial NLRP3 inflammasome activates neurotoxic astrocytes in depression-like [PMID:36288697] Li S, Fang Y, Zhang Y, Song M, Zhang X, Cell reports 2022 0
Biomarker of Neuroinflammation in Parkinson's Disease. [PMID:35456966] Liu TW, Chen CM, Chang KH Int J Mol Sci 2022 0
NLRP3/caspase-1/GSDMD-mediated pyroptosis exerts a crucial role in astrocyte pat [PMID:34877938] Li S, Sun Y, Song M, Song Y, Fang Y, Zha JCI insight 2021 0
Insulin Resistance and Diabetes Mellitus in Alzheimer's Disease. [PMID:34069890] Burillo J, Marqués P, Jiménez B, Gonzále Cells 2021 0
Improvement of glymphatic-lymphatic drainage of beta-amyloid by focused ultrasou [PMID:32999351] Lee Y, Choi Y, Park EJ Sci Rep 2020 0
NLRP3 inflammasome activation drives tau pathology. [PMID:31748742] ["Ising C", "Venegas C", "Zhang S", "Sch Nature 2019 0
Inflammasome inhibition prevents α-synuclein pathology and dopaminergic neurodeg [PMID:30381407] Gordon R, Albornoz EA, Christie DC, Lang Science translational medicine 2018 0
Intraneuronal beta-amyloid aggregates, neurodegeneration, and neuron loss in tra [PMID:17021169] ["Oakley, Holly", "Cole, Sarah L", "Loga The Journal of neuroscience : 2006 0
The amyloid hypothesis of Alzheimer's disease: progress and problems on the road [PMID:12130773] ["Hardy, John", "Selkoe, Dennis J"] Science (New York, N.Y.) 2002 0

Debates (4)

Multi-agent debates referencing this entity

Structured research brief: Stathmin-2 Splice Switching to Prevent Axonal Degener

archived · Rounds: 2 · Score: 0.73 · 2026-04-28

Hypothesis debate: Stathmin-2 Splice Switching to Prevent Axonal Degeneration Ac

closed · Rounds: 4 · Score: 0.49 · 2026-04-27

The ASO therapeutic hypothesis assumes dilncRNAs have targetable conserved struc

closed · Rounds: 4 · Score: 0.69 · 2026-04-21

RNA binding protein dysregulation across ALS FTD AD

closed · Rounds: 4 · Score: 0.50 · 2026-04-13

Related Research

Hypotheses and analyses mentioning ASO in their description or question text

Closed-loop transcranial focused ultrasound to restore hippocampal gamma oscilla

Score: 0.827 · alzheimers · 2026-04-16

## Mechanistic Overview Closed-loop transcranial focused ultrasound to restore hippocampal gamma oscillations via glymph

Real-time gamma-guided transcranial focused ultrasound targeting EC-II SST inter

Score: 0.827 · alzheimers · 2026-04-07

## Mechanistic Overview Real-time gamma-guided transcranial focused ultrasound targeting EC-II SST interneurons to resto

Microglial AIM2 Inflammasome as the Primary Driver of TDP-43 Proteinopathy Neuro

Score: 0.824 · neurodegeneration · 2026-04-05

## Mechanistic Overview Microglial AIM2 Inflammasome as the Primary Driver of TDP-43 Proteinopathy Neuroinflammation in

Astrocyte-Intrinsic NLRP3 Inflammasome Activation by Alpha-Synuclein Aggregates

Score: 0.822 · neurodegeneration · 2026-04-05

## Mechanistic Overview Astrocyte-Intrinsic NLRP3 Inflammasome Activation by Alpha-Synuclein Aggregates Drives Non-Cell-

Mitochondrial DAMPs-Driven AIM2 Inflammasome Activation in Neurodegeneration

Score: 0.805 · neurodegeneration · 2026-04-05

## Mechanistic Overview Mitochondrial DAMPs-Driven AIM2 Inflammasome Activation in Neurodegeneration starts from the cla

Calcium-Dysregulated mPTP Opening as an Alternative mtDNA Release Mechanism for

Score: 0.804 · neurodegeneration · 2026-04-05

## Mechanistic Overview Calcium-Dysregulated mPTP Opening as an Alternative mtDNA Release Mechanism for AIM2 Inflammasom

Targeting the Mechanistic Link Between AQP4 Dysfunction and Ferroptosis Prevents

Score: 0.803 · neurodegeneration · 2026-04-17

## Mechanistic Overview Targeting the Mechanistic Link Between AQP4 Dysfunction and Ferroptosis Prevents Both Cytotoxic

Mitochondrial DNA-Driven AIM2 Inflammasome Activation in Neurodegeneration

Score: 0.803 · neurodegeneration · 2026-04-05

## Mechanistic Overview Mitochondrial DNA-Driven AIM2 Inflammasome Activation in Neurodegeneration starts from the claim

NLRP3 inflammasome amplification across AD and PD proteinopathy

Score: 0.800 · multi · 2026-04-28

Shared mechanism across AD, PD: Misfolded protein stress activates microglial NLRP3; IL-1 beta and inflammasome signalin

Closed-loop transcranial focused ultrasound targeting CA1 PV interneurons with r

Score: 0.797 · alzheimers · 2026-04-07

## Mechanistic Overview Closed-loop transcranial focused ultrasound targeting CA1 PV interneurons with real-time gamma f

Closed-loop transcranial focused ultrasound to restore hippocampal gamma oscilla

Score: 0.767 · alzheimers · 2026-04-12

## Mechanistic Overview Closed-loop transcranial focused ultrasound to restore hippocampal gamma oscillations via somato

Focused Ultrasound with Microbubble Contrast Agents for Antibody CNS Delivery

Score: 0.762 · neurodegeneration · 2026-04-22

## Mechanistic Overview Focused Ultrasound with Microbubble Contrast Agents for Antibody CNS Delivery starts from the cl

ASO-mediated reduction of toxic C9orf72 dipeptide repeat proteins in ALS/FTD

Score: 0.760 · neurodegeneration · 2026-05-01

Antisense oligonucleotides targeting expanded GGGGCC repeats in C9orf72 offer the strongest therapeutic hypothesis by si

Closed-loop focused ultrasound targeting CA1 PV interneurons to restore theta-ga

Score: 0.754 · alzheimers · 2026-04-07

## Mechanistic Overview Closed-loop focused ultrasound targeting CA1 PV interneurons to restore theta-gamma coupling and

Closed-loop focused ultrasound targeting EC-II SST interneurons to restore gamma

Score: 0.748 · alzheimers · 2026-04-05

## Mechanistic Overview Closed-loop focused ultrasound targeting EC-II SST interneurons to restore gamma gating and bloc