disease 1,596 words KG: ent-dise-89aef6a7 2026-03-22
kind:diseasesection:diseasesstate:published
Contents

MSA Genetic Variants

Disease Info
InheritanceAutosomal dominant
SNCAAlpha-synuclein gene duplications and point mutations
GBAGlucocerebrosidase gene mutations (strongest genetic risk factor)
COQ2Coenzyme Q10 biosynthesis gene variants
Other risk genesSHC1, MAPT, STX1B
MechanismMutations promote alpha-synuclein fibrillization
PhenotypeTypical MSA with prominent autonomic failure
SNCA A53TAssociated with familial MSA/PD
SNCA A30PReported in MSA families
N370SMost common GBA mutation in Ashkenazi Jews
L444PSevere mutation associated with Gaucher disease
E326KMissense variant with moderate risk
DatabasesOMIMOrphanetClinicalTrialsPubMed

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