disease 809 words KG: ent-dise-07344cbc 2026-03-24
kind:diseasesection:diseasesstate:published
Contents

APP Arctic Mutation (APP Arctic)

Disease Info
InheritanceAutosomal dominant
GeneAPP (Amyloid Precursor Protein)
Chromosome21q21.3
MutationE693G (Glu693Gly)
cDNA Changec.2128A>G
Discovery1998, Swedish family (Nordstedt et al.)
LocationWithin the Aβ sequence (Aβ position 22)
EffectDoes NOT significantly increase total Aβ production
Primary effectAlters Aβ aggregation properties
ProductionNormal or slightly reduced
AggregationMarkedly accelerated
ProtofibrilsIncreased formation of toxic Aβ protofibrils
DatabasesOMIMOrphanetClinicalTrialsPubMed

Knowledge Graph

Related Hypotheses (14)

Multi-Target Hypothesis: Aβ-Induced Cholinergic Damage is Pa
Score: 0.70
Selective Cholinergic Protection via APP Pathway Modulation
Score: 0.43
SASP-Driven Aquaporin-4 Dysregulation
Score: 0.59
Circadian-Synchronized Proteostasis Enhancement
Score: 0.58
AMPK hypersensitivity in astrocytes creates enhanced mitocho
Score: 0.57

Related Analyses (15)

CRISPR-based therapeutic approaches for neurodegenerative di
neurodegeneration · completed
CRISPR-based therapeutic approaches for neurodegenerative di
neurodegeneration · archived
Autophagy-lysosome pathway convergence across neurodegenerat
neurodegeneration · archived
Protein aggregation cross-seeding across neurodegenerative d
neurodegeneration · archived
Metabolic reprogramming in neurodegenerative disease
neurodegeneration · completed

Related Experiments (25)

Plasma ATN biomarkers across AD continuum in Chilean cohort
clinical · proposed · Score: 0.95
Creation and validation of 3xAD-ChAT-Cre mouse model
validation · proposed · Score: 0.90
Adoptive transfer of TCRAβ-Tregs in AD mouse model
validation · proposed · Score: 0.90
Chi3l1 deletion in APP/PS1 mouse model of Alzheimer's diseas
validation · proposed · Score: 0.95
Anti-ASC antibody intracerebroventricular injection in APP/P
validation · proposed · Score: 0.95