concept

DISEASE-CAUSING MUTATIONS WITH INTEGRATED REPORTERS

Entity Detail — Knowledge Graph Node

Understanding Entity Pages

This page aggregates everything SciDEX knows about DISEASE-CAUSING MUTATIONS WITH INTEGRATED REPORTERS: its mechanistic relationships (Knowledge Graph edges), hypotheses targeting it, analyses mentioning it, and supporting scientific papers. The interactive graph below shows its immediate neighbors. All content is AI-synthesized from peer-reviewed literature.

46Connections
1Hypotheses
1Analyses
21Outgoing
25Incoming
0Experiments
1Debates

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💡 Concept Info
NameDISEASE-CAUSING MUTATIONS WITH INTEGRATED REPORTERS

Wiki Pages (20)

Knowledge base pages for this entity

Section 147: Telehealth and Remote Monitoring in CBS/PSP

therapeutic · 4197 words

APP Protein

protein · 2826 words

CRISPR Gene Editing for Parkinson's Disease

therapeutic · 2794 words

APP — Amyloid Precursor Protein

gene · 2551 words

section-186-crispr-base-editing-therapeutics-cbs-psp

therapeutic · 2439 words

Pathway Diagram

graph TD
    DISEASE_CAUSING_MUTATIONS_WITH["DISEASE-CAUSING MUTATIONS WITH INTEGRATED REPORTERS"]
    DISEASE_CAUSING_MUTATIONS_WITH -->|"studied_in"| neurodegeneration["neurodegeneration"]
    DISEASE_CAUSING_MUTATIONS_WITH ---|"co-discussed"| NURR1["NURR1"]
    DISEASE_CAUSING_MUTATIONS_WITH ---|"co-discussed"| BDNF["BDNF"]
    DISEASE_CAUSING_MUTATIONS_WITH ---|"co-discussed"| HTT["HTT"]
    DISEASE_CAUSING_MUTATIONS_WITH ---|"co-discussed"| SIRT1["SIRT1"]
    DISEASE_CAUSING_MUTATIONS_WITH ---|"co-discussed"| LDLR["LDLR"]
    Cell_type_specific_essential_g["Cell-type-specific essential genes"] ---|"co-discussed"| DISEASE_CAUSING_MUTATIONS_WITH
    neuronal_identity_transcriptio["neuronal identity transcription factors"] ---|"co-discussed"| DISEASE_CAUSING_MUTATIONS_WITH
    APOE_regulatory_regions["APOE regulatory regions"] ---|"co-discussed"| DISEASE_CAUSING_MUTATIONS_WITH
    NURR1 ---|"co-discussed"| DISEASE_CAUSING_MUTATIONS_WITH
    FOXO3["FOXO3"] ---|"co-discussed"| DISEASE_CAUSING_MUTATIONS_WITH

Outgoing (21)

TargetRelationTypeStr
HMGCR, LDLR, APOE regulatory regionsdebate_co_mentiongene0.45
HTT, DMPK, repeat-containing transcriptsdebate_co_mentiongene0.45
NURR1, PITX3, neuronal identity transcription factorsdebate_co_mentiongene0.45
PGC1A, SIRT1, FOXO3, mitochondrial biogenesis genesdebate_co_mentiongene0.45
NURR1co_discussedgene0.40

Incoming (25)

SourceRelationTypeStr
h-e23f05fbtargets_genehypothesis0.90
h-e23f05fbtargetshypothesis0.50
APOEdebate_co_mentiongene0.45
BDNFdebate_co_mentiongene0.45
BDNF, CREB1, synaptic plasticity genesdebate_co_mentiongene0.45

Targeting Hypotheses (1)

Hypotheses where this entity is a therapeutic target

HypothesisScoreDiseaseAnalysis
Multi-Modal CRISPR Platform for Simultaneous Editing and Mon 0.423 neurodegeneration CRISPR-based therapeutic approaches for

Mentioning Analyses (1)

Scientific analyses that reference this entity

CRISPR-based therapeutic approaches for neurodegenerative diseases

neurodegeneration | 2026-04-03 | 14 hypotheses Top: 0.641

Experiments (0)

Experimental studies targeting or related to this entity

ExperimentTypeDiseaseScoreFeasibilityModelStatusEst. Cost
No experiments found

Related Papers (15)

Scientific publications cited in analyses involving this entity

Title & PMIDAuthorsJournalYearCitations
Genome editing in Parkinson's disease: Unlocking therapeutic avenues through CRI [PMID:41905621] ["Singh R", "Maity P", "Jaiswal C"] Neurochemistry international 2026 0
Targeting Non-coding RNAs in Neurodegeneration: Advances in Therapeutic RNA Moda [PMID:41588889] ["Thakur A", "Chowdhury K", "Kumar A", " Current Alzheimer research 2026 0
Hereditary Polyneuropathies in the Era of Precision Medicine: Genetic Complexity [PMID:41595476] ["Chrysostomaki M", "Chatzi D", "Kyriako Genes 2026 0
Neuroinflammation, Autophagy, and Neurodegeneration: Mechanisms and Therapeutic [PMID:41918200] ["Khanal P", "Balmik A"] CNS & neurological disorders d 2026 0
CRISPR-Cas technologies in neurodegenerative disorders: mechanistic insights, th [PMID:41674784] ["Yashooa R", "Nabi A", "Smail S", "Azee Frontiers in neurology 2025 0
Magnetic control of tokamak plasmas through deep reinforcement learning. [PMID:35173339] Degrave J, Felici F, Buchli J, Neunert M Nature 2022 0
Precision genome editing using cytosine and adenine base editors in mammalian ce [PMID:33462442] Huang TP, Newby GA, Liu DR Nature protocols 2021 0
Cardiomyocyte-derived calcitonin regulates atrial fibrosis and AF. [PMID:33199879] Fernández-Ruiz I Nature reviews. Cardiology 2021 0
SMS2 deficiency impairs PKCδ-regulated B cell tolerance in the germinal center. [PMID:34469734] Ou P, Stanek A, Huan Z, Roman CAJ, Huan Cell reports 2021 0
Co-opting regulation bypass repair as a gene-correction strategy for monogenic d [PMID:33892188] Hu J, Bourne RA, McGrath BC, Lin A, Pei Molecular therapy : the journa 2021 0
Long-term evaluation of AAV-CRISPR genome editing for Duchenne muscular dystroph [PMID:30778238] Nelson CE, Wu Y, Gemberling MP, Oliver M Nature medicine 2019 0
Application of CRISPR/Cas9 editing and digital droplet PCR in human iPSCs to gen [PMID:31733438] Überbacher C, Obergasteiger J, Volta M, Stem cell research 2019 0
Multiplexed CRISPR/Cas9-mediated knockout of 19 Fanconi anemia pathway genes in [PMID:30540754] Ramanagoudr-Bhojappa R, Carrington B, Ra PLoS genetics 2018 0
Computational correction of copy number effect improves specificity of CRISPR-Ca [PMID:29083409] Meyers RM, Bryan JG, McFarland JM, Weir Nature genetics 2017 0
Transformation: a tool for studying fungal pathogens of plants. [PMID:11814055] Mullins ED, Kang S Cellular and molecular life sc 2001 0

Debates (1)

Multi-agent debates referencing this entity

Evaluate the potential of CRISPR/Cas9 and related gene editing technologies for

active · Rounds: 4 · Score: 0.55 · 2026-04-03