protein 1,311 words KG: TARDBPPROTEIN 2026-03-23
kind:proteinsection:proteinsstate:published
Contents

TARDBP/TDP-43 Protein

🔬 Protein Info
Gene SymbolTARDBP
Full NameTARDBP/TDP-43
Chromosome1p36
Protein TypeTranscription Factor
Target ClassTranscription Factor
FunctionRNA-binding and transcription regulation, challenging for small molecule targeting
Mechanism of ActionRNA-binding and transcription regulation, challenging for small molecule targeting
Subcellular Localization**Acetylation**: At K263, K331, affects RNA binding
DruggabilityLow (0.43)
Clinical StagePhase III
Molecular Weight43 kDa
Amino Acids4477 aa
PathwaysApoptosis, Autophagy, Immune Response, Oxidative Stress, Tdp-43
UniProt IDA0A087WYY0
GeneCardsTARDBP
Human Protein AtlasTARDBP
Associated DiseasesAD, ALI, ALS, ALS-FTD, Alzheimer
Known Drugs/CompoundsTranscribed Rnas, RAPAMYCIN, rapamycin
InteractionsNTN1, SNRNP70, NTN3, ATG10, PINK1, LC3
SciDEX TargetView Target Profile (7 clinical trials)
SciDEX HypothesesCryptic Exon Silencing Restoration
Cross-Seeding Prevention Strategy
Glycine-Rich Domain Competitive Inhibition (+1 more)
KG Connections1201 knowledge graph edges
DatabasesGeneCardsNCBI GeneHPASTRING

Knowledge Graph

Related Hypotheses (21)

Microglial AIM2 Inflammasome as the Primary Driver of TDP-43
Score: 0.60
Multiplexed Base Editing for Simultaneous Neuroprotective Ge
Score: 0.53
Acid-Degradable LNP-Mediated Prenatal CRISPR Intervention fo
Score: 0.47
Engineered Apolipoprotein E4-Neutralizing Shuttle Peptides
Score: 0.51
Cryptic Exon Silencing Restoration
Score: 0.46

Related Analyses (6)

TDP-43 phase separation therapeutics for ALS-FTD
neurodegeneration · archived
RNA binding protein dysregulation across ALS FTD and AD
neurodegeneration · archived
Mitochondrial transfer between astrocytes and neurons
neurodegeneration · archived
Protein aggregation cross-seeding across neurodegenerative d
neurodegeneration · archived
Circuit-level neural dynamics in neurodegeneration
neuroscience · archived

Related Experiments (13)

TDP-43 mutant mouse model cGAS/STING pathway analysis
validation · proposed · Score: 0.90
TDP-43 mitochondrial invasion and DNA release via mPTP
exploratory · proposed · Score: 0.90
TDP-43 mitochondrial invasion and mtDNA release in iPSC moto
exploratory · proposed · Score: 0.90
cGAS/STING pathway validation in TDP-43 mutant mice
validation · proposed · Score: 0.85
cGAMP biomarker analysis in ALS patient spinal cord samples
exploratory · proposed · Score: 0.80

See Also (15)

Neurodegeneration
disease · KG edge: implicated_in
mitochondrial-dysfunction-neurodegeneration-comparison
disease · Pages share 5 hypotheses
Familial vs Sporadic Neurodegeneration Comparison
disease · Pages share 5 hypotheses
UPenn Observational Research Repository (NCT04715399)
clinical · Pages share 5 hypotheses
Wnt/β-Catenin Signaling Pathway in Neurodegeneration
mechanism · Pages share 4 hypotheses