therapeutic 2,439 words KG: ent-gene-9f063e98
section:therapeuticskind:therapeutictopic:parkinsons
Contents

LRRK2-GBA Combination Therapy for Parkinson's Disease

🔬 Protein Info
Gene SymbolLRRK2
Full NameGBA Combination Therapy for Parkinson's Disease
Chromosome12q12
Protein TypeProtein
Amino Acids2527 aa
PathwaysMAPK
UniProt IDSearch UniProt
GeneCardsLRRK2
Human Protein AtlasLRRK2
ObservationFinding
Population frequency~5% LRRK2-G2019S carriers also carry GBA variants[@[m2020]]
PhenotypeCombined carriers show earlier onset, faster progression[@[m2020]]
Mechanistic synergyBoth pathways converge on lysosomal function[@[m2020]]
Therapeutic rationaleCombination may provide enhanced benefit
Armadillo repeatsProtein-protein interactions
Associated DiseasesALS, Aging, Alzheimer, Alzheimer's disease, Amyotrophic Lateral Sclerosis
Known Drugs/CompoundsRAPAMYCIN, levodopa, Cigarette Smoking, MLi-2, PF-06447475, Environmental Toxicants
InteractionsATG16L1, RB1CC1, GABARAP, ERN1, STAT3, IFNG
KG Connections2480 knowledge graph edges
DatabasesGeneCardsNCBI GeneHPASTRING

Knowledge Graph

Related Hypotheses (30)

Bacterial Enzyme-Mediated Dopamine Precursor Synthesis
Score: 0.36
Engineered Apolipoprotein E4-Neutralizing Shuttle Peptides
Score: 0.51
APOE4-Selective Lipid Nanoemulsion Therapy
Score: 0.49
APOE Isoform Conversion Therapy
Score: 0.44
Lysosomal Positioning Dynamics Modulation
Score: 0.43

Related Analyses (30)

Does TFEB activation directly restore mutant GBA enzyme acti
molecular biology · failed
What is the therapeutic window between GCS inhibition effica
neurodegeneration · failed
GBA-Synuclein Loop: Therapeutic Strategies for Parkinson's D
neurodegeneration · completed
TDP-43 phase separation therapeutics for ALS-FTD
neurodegeneration · archived
APOE4 structural biology and therapeutic targeting strategie
neurodegeneration · archived

Related Experiments (30)

LRRK2/GBA Mutation Carrier Resilience — Why Some Carriers Ne
validation · proposed · Score: 0.46
AAV Serotype Comparison for LRRK2 Knockdown in PD Gene Thera
validation · proposed · Score: 0.46
AAV-LRRK2 IND-Enabling Study Design
clinical · proposed · Score: 0.46
AAV Serotype Comparison for LRRK2 Knockdown in PD
validation · proposed · Score: 0.46
Alpha-Synuclein Aggregation Triggers — Sporadic PD Initiatio
clinical · proposed · Score: 0.46

Key Papers (1)

Randomized control trial of evaluation of Clemastine effects on visual
Clinical neurology and neurosu 2020

See Also (10)

LX1001 Long-Term Follow-up (NCT05400330) - Gene Therapy
clinical · Pages share 4 hypotheses
LX1001 Phase 1/2 Trial (NCT03634007) - Gene Therapy for
clinical · Pages share 4 hypotheses
BEACoN Study - Biomarker Exploration in Aging, Cognitio
clinical · Pages share 4 hypotheses
UPenn Observational Research Repository (NCT04715399)
clinical · Pages share 3 hypotheses
remternetug-anti-amyloid-alzheimers
clinical_trial · Pages share 3 hypotheses

Knowledge Graph (2 edges)

ent-gene-9f063e98 data_in benchmark_ot_ad_answer_key:LRRK2
benchmark_ot_ad_answer_key:LRRK2 data_in ent-gene-9f063e98