therapeutic 983 words KG: ent-gene-2488b5f0 2026-03-22
kind:therapeuticsection:therapeuticsstate:published
Contents

SOD1-Targeting Therapies for ALS

🔬 Protein Info
Gene SymbolSOD1
Full NameTargeting Therapies
Chromosome21q22.11
Protein TypeEnzyme
Functionis a copper/zinc-dependent enzyme that catalyzes the dismutation of superoxide radical (O₂⁻) into molecular oxygen (O₂) and hydrogen peroxide (H₂O₂).
Primary ExpressionMotor cortex, Spinal cord, Widespread throughout CNS
Molecular Weight16 kDa
Amino Acids154 aa
PathwaysAmyloid, Apoptosis, Autophagy, Epigenetic, Er Stress
Ensembl IDENSG00000142168
GeneCardsSOD1
Human Protein AtlasSOD1
ASOCompany
Tofersen (BIIB067)Biogen/Ionis
WVE-004Wave Life Sciences
Associated DiseasesAD, ALS, ALZHEIMER'S DISEASE, AMYOTROPHIC LATERAL SCLEROSIS, ARM, Aging
Known Drugs/CompoundsTOFERSEN, RAPAMYCIN, Lactiplantibacillus plantarum FRT4, Antisense Oligonucleotides, Tofersen, curcumin
InteractionsCALCINEURIN, ATG12, ATG10, GAIN, TNF, PLEKHG5
KG Connections2154 knowledge graph edges
DatabasesGeneCardsUniProtNCBI GeneHPASTRING

Knowledge Graph

Related Hypotheses (23)

Bacterial Enzyme-Mediated Dopamine Precursor Synthesis
Score: 0.59
Engineered Apolipoprotein E4-Neutralizing Shuttle Peptides
Score: 0.72
Metabolic Reprogramming via Microglial Glycolysis Inhibition
Score: 0.67
Selective APOE4 Degradation via Proteolysis Targeting Chimer
Score: 0.79
Competitive APOE4 Domain Stabilization Peptides
Score: 0.78

Related Analyses (15)

Astrocyte reactivity subtypes in neurodegeneration
neurodegeneration · completed
APOE4 structural biology and therapeutic targeting strategie
neurodegeneration · completed
Epigenetic clocks and biological aging in neurodegeneration
neurodegeneration · completed
CRISPR-based therapeutic approaches for neurodegenerative di
neurodegeneration · completed
CRISPR-based therapeutic approaches for neurodegenerative di
neurodegeneration · archived

Related Experiments (29)

s:** - Temporal analysis showing mitochondrial defects prece
falsification · proposed · Score: 0.40
s:** - Single-cell RNA-seq to measure editing efficiency acr
falsification · proposed · Score: 0.40
ALS Regional Onset and Spread: Network-Level Staging Model
clinical · proposed · Score: 0.40
ER-Golgi Secretory Pathway Dysfunction in PD - Experiment De
clinical · proposed · Score: 0.40
Viral and Post-Infectious Mechanisms in ALS — Experiment Des
clinical · proposed · Score: 0.40

See Also (15)

Wnt/β-Catenin Signaling Pathway in Neurodegeneration
mechanism · Pages share 3 hypotheses
WNK1 Kinase in Neurodegeneration
mechanism · Pages share 3 hypotheses
WNK1-Bilirubin Signaling in Neuroinflammation and Neuro
mechanism · Pages share 3 hypotheses
vip-vasoactive-intestinal-peptide-signaling-neurodegene
mechanism · Pages share 3 hypotheses
VEGF Signaling and Cerebral Angiogenesis in Neurodegene
mechanism · Pages share 3 hypotheses

Knowledge Graph (2 edges)

ent-gene-2488b5f0 data_in benchmark_ot_ad_answer_key:SOD1
benchmark_ot_ad_answer_key:SOD1 data_in ent-gene-2488b5f0

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